Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...

Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

Men with SMA are likely to have fertility issues, and patients with more severe motor impairments have lower sperm counts, ...

Scholar Rock aims for a 2025 launch of apitegromab in SMA, expecting $2 billion in global revenue and significant growth from upcoming trials and favorable data.

Crystal Rondeau’s muscle wasting disease has left her with only one finger to press an alarm button or send a text. The ...

Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...

Advocates rallied outside the State House on Tuesday for special education funding.The group urged lawmakers to allocate more ...

who are living with Spinal Muscular Atrophy (SMA) with the support of her mother, sister and teacher. Ms. Keya was felicitated by the Visakha Rasagna Vedika, a cultural organisation, at the Public ...

Upper House member Haris Beeran has said the current costs of medicines approved for SMA are 'beyond the reach of the central ...