This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

In this review of RNA therapies, we paint an overview of what’s going on in a field that is addressing a number of diseases.

RFK Jr.'s comments about the gene-editing technology raise a question about how he would regulate it as head of HHS.

we now have the tools to directly change someone's DNA—this has paved the way for gene editing as a type of gene therapy. It is done using the CRISPR-Cas9 system, which was created after ...

Could viral infections play a role in Huntington's disease? Research suggests Apolipoprotein B mRNA editing catalytic ...

The president announced a major AI investment project, which Oracle Chairman Larry Ellison said could be used to cure cancer.

APOBEC enzymes, which normally help fight viral infections by mutating viral DNA, cause repeat expansions and are unusually ...

People genetically susceptible to Huntington's disease often see their movement, mood, and cognition decline slowly over time ...

People genetically susceptible to Huntington's disease often see their movement, mood, and cognition decline slowly over time.

Verve Therapeutics has started dosing patients in a phase 1b trial of its in vivo gene-editing drug for high cholesterol, designed to permanently switch off the PCSK9 gene with a one-shot treatment.