In recent years, a growing understanding of myotonic dystrophy type 1 (DM1 ... making it the most common adult-onset muscular dystrophy. We believe that the market opportunity for a new DM1 ...
Other symptoms may include: Often children with Becker muscular dystrophy can walk. As they get older they may need to use a cane or wheelchair to get around. The symptoms of myotonic dystrophy ...
The disease limits their life expectancy to just 20 years old. The most common form in adults is Myotonic muscular dystrophy. Apart from the muscle wasting, it can affect other organs such as the ...
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Investor's Business Daily on MSNAvidity Biosciences, Up 441%, Nears Another Record High As Dystrophy Space Heats UpMuscles in the face, shoulders ... Biosciences is also testing treatments for myotonic dystrophy type 1 and a subset of ...
It is the third most common muscular dystrophy, after myotonic dystrophy and dystrophinopathies ... Other symptoms may include: Non-Muscle Features: Some individuals develop retinal vascular ...
Objectives: To determine risk factors for cardiac complications in patients with myotonic dystrophy, and to determine whether permanent cardiac pacemakers may be beneficial in the treatment of ...
Please provide your email address to receive an email when new articles are posted on . The FDA has granted fast-track designation to an investigational antisense oligonucleotide to treat ...
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