Medscape13 年
A Successful Early Trial of Oligomer Treatment for Duchenne Muscular Dystrophy
Each patient was treated with 12 weekly IV infusions of a phosphorodiamidate morpholino oligomer, AVI-4658, at doses ranging from 0.5 mg/kg to 20 mg/kg. A total of 19 patients were enrolled in the ...
Zacks.com on MSN5 个月
Dyne Reports Mixed Data From DMD Study, Key Executives Step Down
DYNE-251 consists of a phosphorodiamidate morpholino oligomer (PMO) conjugated to a fragment antibody that binds to the ...