Scholar Rock aims for a 2025 launch of apitegromab in SMA, expecting $2 billion in global revenue and significant growth from upcoming trials and favorable data.

Creatinine, a byproduct of muscle function, may be more sensitive in tracking SMA progression and response to treatment than ...

Advocates rallied outside the State House on Tuesday for special education funding.The group urged lawmakers to allocate more ...

Crystal Rondeau’s muscle wasting disease has left her with only one finger to press an alarm button or send a text. The ...

Exercise can enhance the lives of people with spinal muscular atrophy (SMA) by improving or maintaining function and quality of life. This is accomplished through activities that help to maintain or ...

Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

Known online as Squirmy and Grubs, YouTubers Hannah and Shane Burcaw have over 1.8 million subscribers. The married ...

Accessible travel blog founder Cory Lee is committed to helping other wheelchair users travel the world freely.

Scholar Rock , a late-stage biopharmaceutical company focused on advancing innovative treatments for spinal muscular atrophy (SMA), cardiometabolic disorders, and other serious diseases where protein ...

In a new essay collection, the influencer couple Shane and Hannah Burcaw peel back the layers of “interabled” relationships, ...