This repository contains the R scripts for bulk RNAseq of lung biopsies from mice infected with Pseudomonas aeruginosa with/without anti-ANGPTL4 ASO treatment. The study aims to establishes ...

You can create a release to package software, along with release notes and links to binary files, for other people to use. Learn more about releases in our docs.

Children's Mercy Kansas City has achieved a significant advancement toward the treatment of rare genetic diseases through the ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

The Massachusetts based biotech will now press ahead with human trials for its antisense oligonucleotide (ASO) therapy, ...

New research published in the Journal of Chromatography A examines the effect of flow rate on plate height and resolution for antisense oligonucleotides (ONs) under hydrophilic interaction liquid ...

A drug that halts an AIDS-related eye infection could be the first antisense therapy to reach the market. However, whether the drug can truly be called "antisense" depends on some specifics--such as ...

In trials at University College London Hospitals (UCLH), an ASO is being used to target the mutated gene that results in the ...

Visit the Clinical Trial Finder to browse for genetic therapy clinical trials that are currently enrolling. Antisense oligonucleotide (ASO) therapy is being explored to correct the effects of rare ...

Massachusett-based Stoke Therapeutics STOK is making rapid progress with the development of zorevunersen (STK-001), its ...

Sanofi has entered into a collaboration and license agreement with Alloy Therapeutics to develop an antisense oligonucleotide (ASO) therapy targeting a single, undisclosed central nervous system ...

This is the latest venture for Amylyx into the ALS field after its previous therapy Relyvrio was pulled from the market in ...