Achondroplasia, which affects around one in 20,000 babies, has just one approved treatment: BioMarin’s Voxzogo. However, new investigational treatments are vying to compete in the area.
I don’t know if it’s an inherited trait, but I come from a long line of collectors who were both inquisitive and acquisitive,” Beth Hutchens says. “Sometimes it can be a problem.” While family members ...