Dysautonomia refers to a group of disorders involving nerves that control heart rate, breathing, and other involuntary functions. Dysautonomia can be difficult to diagnose, in part because ...
Dysautonomia refers to a group of disorders involving nerves that control heart rate, breathing, and other involuntary functions. Dysautonomia can be difficult to diagnose, in part because symptoms ...
Tikun Therapeutics Inc. has obtained U.S. orphan drug and rare pediatric disease designations for its programs in familial dysautonomia, namely its rAAV2-U1a-hELP1 gene replacement therapy for the ...