The evolution of cell and gene therapy is reshaping drug discovery, providing new hope for rare diseases and cancer through innovative gene editing approaches.

Archived copies of the webcasts will be available for up to one year on the “Investors” section of the 4DMT website at https://ir.4dmoleculartherapeutics.com/events.

First patient dosed in the pediatric cohort of the Phase 1/2 trial of OPGx-LCA5; initial data on the cohort anticipated by Q3 2025New 12-month ...

Organoids were cultured from healthy donor iPSC sources and differentiated using the human iPSC-derived Cerebral Organoid ...

Accurate monitoring of particle size and growth is essential to ensure scalability in the development of transfection vectors ...

Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

On November 15, the U.S. Food and Drug Administration (FDA) released its final rule on Requirements for Additional Traceability Records for Certain Foods (Food Traceability Rule). The rule defines ...

WEDNESDAY, Feb. 5, 2025 (HealthDay News) -- The U.S. Food and Drug Administration has approved Susvimo (ranibizumab) 100 mg/mL for treating diabetic macular edema. Susvimo is the first and only ...

This September, the U.S. Food and Drug Administration (FDA) released its proposed update to the nutrient content claim “healthy.” Used in food package labeling, the term is intended to help busy ...

From gambling mercenaries to vicious criminals and even space felines, Citizen Sleeper 2 has some wild and memorable characters.

A set of 5862 free MIT-licensed high-quality SVG icons for you to use in your web projects. Each icon is designed on a 24x24 grid and a 2px stroke. If you load an icon as an image, you can modify its ...

Scholar Rock is asking the U.S. Food and Drug Administration (FDA) to approve apitegromab, its experimental add-on therapy designed to boost motor function in people with spinal muscular atrophy (SMA) ...