The founder of our Basic Sciences Division, Dr. Hal Weintraub ... A cell's functions are determined by which genes are turned on, how strongly and when. Major changes in gene expression underlie ...
Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...
The US gene therapy company Regenxbio and the Japanese firm Nippon Shinyaku have joined forces to boost the development and commercialization of Regenxbio’s gene therapies RGX-121 for the treatment of ...