Genetic Swiss Army Knife: New Tool For Gene Editing And Therapy
This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...
Gene therapy may be 'one-shot stop' for rare bone disease
For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...
The Scientist1d
A Nanoparticle Delivery System for Gene Therapy
Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose unique challenges for gene therapy applications. For ...
News Medical on MSN6h
New gene therapy shows promise for lifelong treatment of hypophosphatasia
For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that must be delivered by injection three-to-six times each week.
Narayana Nethralaya to cut gene therapy costs for eye diseases by 80%
BENGALURU: Bengaluru-based Narayana Nethralaya is developing gene therapy solutions that could drastically reduce the cost of ...
Managed Healthcare Executive3d
Gene Therapy’s Pipeline Has a Steady Flow of More Than 2,000 Candidates
The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...
openaccessgovernment1d
Gene therapy offers new hope for sickle cell disease patients
A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...