Legit on MSN3 天
Relief for SS People as Scientists Finally Discover 'Potential Cure' for Sickle Cell Disease
NHS approves £1.65m gene therapy for sickle cell disease, offering a potential cure. A milestone for patients, especially in ...
Nature6 年
Growing pains for gene therapy manufacturing
In December 2017, the US Food & Drug Administration (FDA) approved Luxturna from Spark Therapeutics — the first gene therapy to win market approval in the US. Several other gene therapy programs ...
Groundbreaking £1.65m gene-editing therapy approved for NHS use offers hope to severe ...
The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...