Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...

Growing advancements in haemophilia treatment underscore a significant shift toward targeted and long-lasting therapeutic ...

For centuries, hemophilia was a dangerous genetic disorder with no treatment. Children with hemophilia often didn't make it to adulthood, since a bump or fall could cause massive internal bleeding.

The recent announcement by the government to provide free medicines for hemophilia patients is a welcome step forward in ...

Pfizer’s anti-TFPI antibody marstacimab has been approved by the FDA to treat haemophilia, becoming the pharma group’s second new therapy for the blood disorder this year. Marstacimab will be ...

Sangamo chief executive Sandy Macrae has said the company is "surprised and extremely disappointed" by Pfizer's decision to hand back rights to its experimental gene therapy for haemophilia A ...

UC San Diego announced that it is offering a newly Food and Drug Administration-approved gene therapy for hemophilia B, a ...

Financial writer discusses MGX's gene editing technology, cash runway, and lack of clinical data for potential future ...

After having a bad experience getting three vaccines at once, columnist Jennifer Lynne says that next time, she'll space them apart.

Researchers found that pediatric male patients with hemophilia are at a greater risk of falls due to poor dynamic balance.

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

Roche has reported a 7% increase in full-year 2024 sales at constant exchange rates (CER), reaching CHF 60.5bn ($66.9bn). The ...