Leah Messer is opening up about navigating her daughter Ali's muscular dystrophy as the 15-year-old takes a big step in her life: high school. In an interview with TooFab ahead of the new season ...

2025 could be a breakout year for the Duchenne muscular dystrophy space. Although several therapies have entered the market in recent years, there is still considerable unmet need for the 15,000 ...

has granted Fast Track designation for DYNE-101 for the treatment of myotonic dystrophy type 1 (DM1). DYNE-101 is currently being evaluated in the ongoing Phase 1/2 ACHIEVE global clinical trial.

Please provide your email address to receive an email when new articles are posted on . The FDA has granted fast-track designation to an investigational antisense oligonucleotide to treat ...