For recurrent respiratory papillomatosis (RRP), novel gene therapy to jump-start immunity to the human papillomavirus (HPV) ...

Gene therapy, a revolutionary approach to treating disease by modifying a person's genes, is one of the most transformative developments in healthcare today. In certain cases, it can offer a cure for ...

Life-changing gene therapies for hemophilia have become available, yet many patients and providers have not yet rushed to try ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

A pivotal experience in a Hopkins lab inspired Roger Hajjar, '86, to forge a career at the intersection of engineering and ...

Jason Foster, CEO of Ori Biotech, discusses the difficulties preventing more widespread adoption of these advanced therapies.

The companies will work together by using the codon-optimized BBS1 AAV9 vector to minimize the vision loss caused by the ...