Taysha Gene Therapies offers hope for Rett syndrome with innovative treatment, strong trial results, and promising regulatory ...

This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

For recurrent respiratory papillomatosis (RRP), novel gene therapy to jump-start immunity to the human papillomavirus (HPV) ...

The companies will work together by using the codon-optimized BBS1 AAV9 vector to minimize the vision loss caused by the ...

New gene editing methods have been introduced in the country, bringing new hope to couples who tested positive for certain ...

Don't Die: The Man Who Wants to Live Forever is Netflix's new documentary film about Bryan Johnson's anti-aging attempts, and here's what the Minicircle gene therapy company actually is.

Gene therapy, a revolutionary approach to treating disease by modifying a person's genes, is one of the most transformative developments in healthcare today. In certain cases, it can offer a cure for ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

Life-changing gene therapies for hemophilia have become available, yet many patients and providers have not yet rushed to try ...

A pivotal experience in a Hopkins lab inspired Roger Hajjar, '86, to forge a career at the intersection of engineering and ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.