The American Cancer Society estimates that 83,000 new cases of bladder cancer will be diagnosed this year, with nearly 17,000 ...

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that ...

The bill would implement a moratorium for a decade. “I am not against vaccination in any way,” the freshman lawmaker said.

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

The California Institute for Regenerative Medicine has awarded a $6 million grant to USC investigators pioneering a new first ...

Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose unique challenges for gene therapy applications. For ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

A pivotal experience in a Hopkins lab inspired Roger Hajjar, '86, to forge a career at the intersection of engineering and ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.

Previous research has shown that voretigene neparvovec administered subretinally early in childhood for RPE65-mediated ...