Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

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A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Spinal muscular atrophy, SMA, a genetic neuromuscular disorder with progressive muscle wasting due to mutation in the SMN1 gene, deficiency in SMN protein, and loss of motor neurons, 3D illustration ...

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

Quebec has no age restrictions. A doctor previously told CBC News around 90 per cent of his adult patients with spinal muscular atrophy in the province have benefited from risdiplam.

Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...