Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

Learn more about whether Ionis Pharmaceuticals, Inc. or PTC Therapeutics, Inc. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

CAMBRIDGE, Mass. - Scholar Rock (NASDAQ: SRRK), a biopharmaceutical company with a market capitalization of $3.96 billion and an impressive 362.73% stock price surge over the past six months, ...

MED-EL USA, a pioneer in hearing implant technology, today announced that new and existing MED-EL hearing implant recipients can access a year of the Meludia online music training program at no cost.

Scholar Rock , a late-stage biopharmaceutical company focused on advancing innovative treatments for spinal muscular atrophy (SMA), cardiometabolic disorders, and other serious diseases where protein ...

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

Life After, a documentary debuting today at Sundance, examines Elizabeth Bouvia's story, and conflicts between right-to-die ...

MDA launches 75th Anniversary campaign and premieres new public service announcement (PSA) to mark 75 years of impact in the ...

Filmmaker Reid Davenport weaves a powerful first-person perspective with a journalistic investigation about disability ...

One-year-old Asmika Das from Ranaghat, Nadia, is suffering from a fatal disease called Spinal Muscular atrophy.

Roche has reported positive results from the second year of the EMBARK Phase III trial of Elevidys (delandistrogene moxeparvovec), the first approv ...

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...