Solid Biosciences' SGT-003 gene therapy showed strong dystrophin expression, muscle health improvements, and no serious safety concerns in early trial data.

Pathogen-associated molecular patterns (PAMP) and damage-associated molecular patterns (DAMP) can activate toll-like receptors (TLR) on platelets. CLEC-2 indicates C-type lectin-like receptor 2; GPVI, ...

Glanzmann thrombasthenia (GT) is a rare haematological disorder with abnormal platelet surface receptor glycoprotein IIb/IIIa, resulting in faulty platelet aggregation. Patients with GT may present ...

For the past month, local basketball programs have teamed up to raise awareness and spread hope for 9-year-old Autumn and ...

Lymphopenia can have many causes, such as viral or bacterial Infections, medications, inherited conditions, or autoimmune disorders. When treatment is needed ... This is followed by thrombocytes ...

Lainie Jones, a 41-year-old woman from Florida, has Li-Fraumeni Syndrome (LFS), an genetic disorder that leads to an increased risk of certain cancers, and is now battling glioblastoma, the 7th type ...

A newly released Cleveland Clinic online survey of 251 Florida adults found that many don’t know what can harm or improve ...

An Italian foundation that helped a young boy overcome Wiskott-Aldrich syndrome becomes the first non-profit in the world to ...

While blood clots serve an essential purpose in healing injuries, they can transform into life-threatening conditions when ...

Genetic engineering is the act of modifying the genetic makeup of an organism. Modifications can be generated by methods such as gene targeting, nuclear transplantation, transfection of synthetic ...

Endosomal recycling is a branch of intracellular membrane trafficking that retrieves endocytosed cargo proteins from early and late endosomes to prevent their degradatio ...