sicklecellanemianews2 天
First patient enrolled in Phase 1 trial testing fostamatinib for SCD
The first patient has been enrolled in a Phase 1 trial by the NHLBI that's evaluating fostamatinib as a treatment for sickle ...
National Institute for Health and Care Excellence6 天
Groundbreaking one-off gene therapy approved for severe sickle cell disease
People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...
The Punch on MSN3 天
Groundbreaking sickle cell disease treatment approved for English NHS
Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as ...
Rolling Out2 天
This medical breakthrough could change sickle cell forever
New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.
pharmaphorum4 天
Pfizer pulls sickle cell med Oxbryta off market after deaths
It's a blow to the SCD community, as Oxbryta (voxelotor) was the first drug to reach the market that prevented sickle haemoglobin (HbS) polymerisation, the molecular basis of sickling and ...