New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Apple has chided a newly available pornography app available in the European Union, and warned that the bloc’s digital rules ...

Health systems across the country are making it easier for primary care clinicians to order genetic tests for patients who ...

Texas House Democrats gathered on Monday to issue a call for action concerning Senate Bill 2, a new attempt at school choice ...

In Pennsylvania and nationwide, heart disease is the leading cause of death. While certain lifestyle factors, like smoking ...

This study provides a valuable new resource to investigate the molecular basis of the particular features characterizing the pipefish embryo. The authors found both unique and shared gene expression ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.

The three-term Republican governor touted his achievements on border security as he calls for more tax cuts and more money ...

During a routine test, Johnny's middle school nurse discovered his severe scoliosis, a prevalent symptom of Marfan. This unexpectedly set his family on a path to uncover his underlying diagnosis at ...

A team of researchers has successfully engineered a bi-paternal mouse - a mouse with two dads - that survived until adulthood ...

Narfunda Ross was the guest speaker at Monday’s meeting of the Valley Lions Club, held at San Marcos Restaurant. She talked ...